A lifesaving therapy for children with a rare disease is now the world’s most expensive drug, raising questions about access

A lifesaving therapy for children with a rare disease is now the world’s most expensive drug, raising questions about access | CNN
A new gene therapy for the fatal genetic disorder metachromatic leukodystrophy, or MLD, will carry a wholesale price of $4.25 million, its manufacturer announced Wednesday, making it the world’s most expensive medicine.